НАСЛЕДСТВЕННЫЕ БОЛЕЗНИ
ТЕРАПИЯ

А



OBESITY
  • DRUG TARGETS
      ◊ Lipid metabolic enzymes
  • GENE THERAPY
      ◊ BMP4 Gene Therapy Protects from Obesity
      ◊ CRISPR-mediated gene editing to rescue haploinsufficient obesity syndrome

      ◊ CRISPR-mediated gene editing to rescue haploinsufficient obesity syndrome

      ◊ The promise of new anti-obesity therapies arising from knowledge of genetic obesity traits
    • OCULAR DISEASES
  • GENE THERAPY
      ◊ Ocular Gene Therapy: With Focus on Current Clinical Trials
  • THERAPEUTIC APPROACh
      ◊ Therapeutic landscape for inherited ocular diseases: current and emerging therapies
    • ONCOTHERAPY
  • DELIVERY OF GENE EDITING ELEMENTS
      ◊ Ionizable lipid-assisted efficient hepatic delivery of gene editing elements for oncotherapy ORAL CANCER
  • VITAMIN D in the PREVENTION AND TREATMENT
      ◊ Vitamin D in the Prevention and Treatment of Oral Cancer:
    • OSTEOARTRITIS
  • CELL TERAPY
      ◊ Efficacy and Safety of Genetically Engineered Allogeneic Human Chondrocytes Expressing TGF-β1 by knee osteoartritis
  • GENE TERAPY
      ◊ Non-Viral Gene Therapy Systems for Orthopaedics
      ◊ Nav1.7 as a chondrocyte regulator and therapeutic target for osteoarthritis
      ◊ The evolving landscape of gene therapy strategies for the treatment of osteoarthritis
    • OSTEOPETROSIS
  • THERAPY
      ◊ Many Genes: Implications for the Treatment of Osteopetroses
    • OSTEOPOROSIS
  • NEW DRUG
      ◊ Teriparatide
    • OVERACTIVE BLADDER
  • GENE THERAPY
      ◊ Gene Therapy and Overactive Bladder