НАСЛЕДСТВЕННЫЕ БОЛЕЗНИ
ТЕРАПИЯ



И

ICHTHYOSIS INHERITED

  •   ◊ Gene Therapy of Autosomal Recessive Congenital Ichthyosis and Other Types of Inherited Ichthyosis
    • IDIOPATHIC PULMONARY FIBROSIS
  • THERAPY
      ◊ Gene therapy strategies for idiopathic pulmonary fibrosis
  • GENE THERAPY
      ◊ model to evaluate regulatory T cells in gene therapy
    • IMMUNEDEFICIENCY
  • GENE THERAPY
      ◊ T cell gene therapy to treat immunodeficiency
      ◊ Therapy for Inborn Errors of Immunity
    • IMMUNE TOLERANCE
  • Cas9-DIRECTED
      ◊ model to evaluate regulatory T cells in gene therapy
    • INCLUSION BODY MYOPATHY, PAGET DISEASE WITH FRONTOTEMPORAL DEMENTIA (IBMPFD)
  • THERAPEUTIC INTERVENTION
      ◊ Valosin-containing protein (VCP/p97) inhibitors
    • INHERITED RETINAL DYSTROPHIES
  • GENE THERAPY
      ◊ Retinal gene therapy
    • INFARCT
  • POST-INFARCT ARRHYTHMIAS
      ◊ Overexpression of Cx43 in cells of the myocardial scar: Correction of post-infarct arrhythmias
  • CRISPR/Cas9-EDITING
      ◊ Dynamics and function of transplanted human urinary-induced pluripotent stem cell-derived cardiomyocytes
    • INFECTIOUS DISEASE
  • CRISPR THERAPY
      ◊CRISPR-based strategies in infectious disease diagnosis and therapy

    INFERTILITY
  • IVF
      ◊ Genetics in reproductive endocrinology and infertility

    • INFLAMMATORY DISEASE
  • THERAPEUTIC INTERVENTION
      ◊ Targeting IL-1
      ◊ P38 map kinases
      ◊ Mechanism to terminate inflammasome activity
      ◊ Gene editing for inflammatory disorders
    • INTELLECTUAL DISABILITY
  • THERAPY
      ◊ gene editing
    • INTERACTIONS PROTEIN-PROTEIN

  •   ◊ Modulation as Novel Therapeutics
    • INTERVERTEBRAL DISK DEGENERATION
  • GENETIC THERAPY
      ◊ Genetic Therapy for Intervertebral Disc Degeneration
  • CELL THERAPY
      ◊ Differentiation of human induced pluripotent stem cells into nucleus pulposus-like cells Treatment of Intervertebral Disk Disease by the Administration of mRNA Encoding a Cartilage-Anabolic Transcription Factor
    • INTRAPERITONEAL TUMORS
  • GENE THERAPY
      ◊ Enzyme-Responsive Charge-Reversal Polymer Mediated Effective Gene Therapy for Intraperitoneal Tumors
    • IPEX SYNDROME
  • GENE THERAPY
      ◊ Gene editing FOXP3 gene in HSPCs and IPEX patient T cells
    • ISCHEMIC HEART DISEASE
  • THERAPY
      ◊ Approaches to therapeutic angiogenesis for ischemic heart disease
      ◊ ISCHEMIC BRAIN DISEASE
  • THERAPY A NeuroD1 AAV-Based Gene Therapy for Functional Brain Repair after Ischemic Injury