SARCOPENIA

GENE THERAPY
  ◊ Improvement sarcopenia by AAV/SaCas9-mediated myostatin gene editing in aged mice

SKIN DISEASES

GENE THERAPY
  ◊ Advances in gene therapy and their application to skin diseases
  ◊ Ex vivo gene modification therapy for genetic skin diseases—recent advances in gene modification technologies and delivery

SICKLE CELL DISEASE

CELL-BASED THERAPY
  ◊ cell-based therapy for adult sickle cell disease

THERAPY
  ◊ New Therapeutic Options for the Treatment of Sickle Cell Disease
  ◊ NRF2 gene silencing inhibits fetal hemoglobin expression in sickle cell disease
  ◊ Gene editing strategies for human β-globin (HBB) gene mutations

GENE THERAPY
  ◊Gene therapy for sickle cell disease
  ◊ Gene therapy approach to sickle cell disease
  ◊ CRISPR/Cas9 gene editing for curing sickle cell disease
  ◊Current state of gene therapy in sickle cell disease
  ◊Role of gene therapy in sickle cell disease

GENE THERAPY and HEMATOPOIETIC STEM CELL TRANSPLANTATION
  ◊comparing allogeneic hematopoietic stem cell transplant to gene therapy in sickle cell disease

SPLICING STRATEGY

RNA TRANS-SPLICING THERAPY
  ◊ Correct human generalized severe epidermolysis bullosa simplex

SPINAL CORD INJURY

GENE THERAPY
  ◊ Immune-evasive gene switch enables regulated delivery of chondroitinase after spinal cord injury
  ◊ The potential of gene therapies for spinal cord injury repair

STEM CELL THERAPY
  ◊ Vascular endothelial growth factor activates neural stem cells after spinal cord injury

SPINA BIFIDA
  ◊ Spina Bifida: A Review of the Genetics, Pathophysiology and Emerging Cellular Therapies

SPINAL AND BULBAR MUSCULAR ATROPHY

RESCUES POLYGLUTAMINE-DEPENDET PHENOTYPES
  ◊ Leuprorelin

SPINAL MUSCULAR ATROPHY

THERAPY
  ◊Скрининг новорожденных и лечение Duchenne muscular dystrophy и spinal muscular atrophy
  ◊ Therapeutic Developments for the Treatment of Spinal Muscular Atrophy: Restoring SMN Expression

GENE THERAPY
  ◊gene therapy in spinal muscular atrophy and Duchenne muscular dystrophy

SPLICE INTERVENTION

ANTISENSE-MEDIATED THERAPY
  ◊ Antisense-mediated splice intervention to treat human disease

SPONGIFORM ENCEPHALOPATHY

THERAPEVTIC APPROACHES
  ◊ superoxide dismutase-catalase mimetics

STATIN THERAPY

CHOLESTEROL REDUCTION
  ◊ Pravastatin

OTHER EFFECTS
  ◊ On breast cancer cells

STEM CELLS

NEURAL STEM/PRECURSOR CELLS
  ◊ Therapeutic potential

NEURODEGENERATIVE DISEASES THERAPY
  ◊ Replacement therapies
  ◊ Stem-cell-based transplantation

STEM-CELL-BASED THERAPIES
  ◊ Tolerance strategies

STEM-CELL-BASED THERAPIES FOR BLOOD DISEASE
  ◊ Haematopoietic stem cells

STEM-CELL-BASED THERAPIES FOR HEART DISEASE
  ◊ Therapeutic potential
  ◊ Lessons

STERILITY

THERAPY
  ◊ Removal of additional sex chromosome by trisomic mice

SYNTHETIC TRANSCRIPTION FACTORS

CELL and GENE THERAPY
  ◊ Programmable synthetic receptors: the next-generation of cell and gene therapies
  ◊ Synthetic transcription factor engineering for cell and gene therapy

SYSTEMIC LUPUS ERYTHEMATOSUS

THERAPY
  ◊ Exosomes as Drug Delivery Systems for Treatment of Systemic Lupus Erythematosus

SUICIDE THERAPY

GENOMIC SAFE HARBORS
  ◊ Human Genomic Safe Harbors and the Suicide

SURFACTANT DYSFUNCTION

GENOTHERAPY
  ◊ Gene Therapy Potential for Genetic Disorders of Surfactant Dysfunction